| Trade name |
Active ingredients |
Pharmaceutical company |
|
Ammonapse | Phenylbutyrate Sodium | Orphan Pharmaceutical |
| Antizol | Fomepizole | Orphan Pharmaceutical; IDIS World Medicines; Medisource; Paladin Laboratories; Tzamal Pharma |
| Betapred | Betamethasone Sodium Phosphate | Orphan Pharmaceutical |
| Carbaglu | Carglumic Acid | Orphan Pharmaceutical |
| Cystadan | Betaine Anhydrous | Orphan Pharmaceutical; Tzamal Pharma |
| Cystagon | Cysteamine Bitartrate | Orphan Pharmaceutical; Mylan |
| Fosrenol | Lanthanum (Lanthanum Carbonate Hydrate) | Orphan Pharmaceutical; DSM Pharmaceuticals; Fahrenheit; Hind Wing; Invida; Opopharma; Shire; Zuellig Pharma |
| Normosang | Hemin Human | Orphan Pharmaceutical; Leiras; Stauffacher Apotheke |
| Orfadin | Nitisinone | Orphan Pharmaceutical; Apoteket Produktion & Laboratorier; Rare Disease Therapeutics |
| Pedea | Ibuprofen | Orphan Pharmaceutical; Merckle; Nycomed |